What You Should Know about Clinical Research Studies

What is a Clinical Research Study?

A clinical research study is a carefully designed research study conducted in people to determine if an investigational medicine is safe and effective. We encourage patients to speak first with their physician about their eligibility to enroll in a clinical trial. New medicines are made possible by the volunteers who participate in clinical trials. Thank you for your consideration of this important study.

Why Should I Participate?

While you may or may not benefit directly from this study, your participation could play an important role in the health of future generations with Alpha-1.

How Long Will Study Participation Last?

Your study participation could last approximately 11–16 weeks depending on whether or not you have ever been on augmentation therapy.

Can I Leave the Study if I Change my Mind?

Taking part in this study is your choice, and you may leave the study at any time for any reason. You should consult the study doctor and staff about concerns and questions you have at any time during the study.

What Should I Expect?

Before you can take part in this study, you will first need to attend the screening visit(s) for initial tests and assessments to see if you are eligible to participate. After all necessary tests and assessments have been completed, and if you are eligible to participate, you may enter the study and receive the investigational medication.

What is the Investigational Medication?

The medication being investigated in the Alpha-1 Study is an oral pill (not given through an infusion or inhaled) investigational medication. You will receive either the investigational medication or placebo. A placebo is an inactive pill that looks like the investigational medication but does not contain any active medication. You have an 80% chance of receiving active medication. Neither you nor the study doctor will know if you are receiving the investigational medication or placebo.

Learn more about the Alpha-1 Study.

See If You May Qualify